| Id |
Subject |
Object |
Predicate |
Lexical cue |
| TextSentencer_T1 |
0-186 |
Sentence |
denotes |
Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with CD34+ selected autologous peripheral blood cells transduced with a human ADA gene. |
| TextSentencer_T2 |
187-262 |
Sentence |
denotes |
Amendment to clinical research project, Project 90-C-195, January 10, 1992. |
| TextSentencer_T3 |
263-530 |
Sentence |
denotes |
Significant increases in lymphocyte adenosine deaminase activity, T cell numbers and immune function have been achieved in the two children with SCID thus far treated with autologous T cells genetically-corrected by retroviral-mediated insertion of a normal ADA gene. |
| TextSentencer_T4 |
531-811 |
Sentence |
denotes |
Although the data obtained to date demonstrate that the use of ADA gene corrected peripheral T cells appears to be an effective treatment for ADA(-)SCID, it is theoretically preferable to try to develop a treatment for these children that will result in stem cell gene correction. |
| TextSentencer_T5 |
812-1102 |
Sentence |
denotes |
The genetic correction of T cell progenitors with long-term immune reconstituting ability would be more desirable because repeated infusions of genetically altered cells should not be necessary and the generation of a more complete repertoire of T cell specificities might also be possible. |
| TextSentencer_T6 |
1103-1225 |
Sentence |
denotes |
Furthermore, the present treatment protocol involves indefinite continuation of enzyme replacement treatment with PEG-ADA. |
| TextSentencer_T7 |
1226-1428 |
Sentence |
denotes |
The demonstration of ADA gene expression in the progeny of transduced stem cells may simplify the decision concerning cessation of this very costly enzyme treatment (approximately $250,000/yr./patient). |
| TextSentencer_T8 |
1429-1642 |
Sentence |
denotes |
Recent evidence suggests that a small fraction of bone marrow or peripheral blood mononuclear cells bearing the CD34 antigen contains hematopoietic stem cells with both lymphoid and myeloid reconstituting ability. |
| TextSentencer_T9 |
1643-1914 |
Sentence |
denotes |
We propose in this amendment to supplement the infusion of human ADA gene-transduced autologous T cells in children with ADA(-)SCID with autologous peripheral blood CD34+ cells transduced with a second, readily distinguishable ADA vector.(ABSTRACT TRUNCATED AT 250 WORDS) |
| T1 |
0-186 |
Sentence |
denotes |
Treatment of severe combined immunodeficiency disease (SCID) due to adenosine deaminase deficiency with CD34+ selected autologous peripheral blood cells transduced with a human ADA gene. |
| T2 |
187-262 |
Sentence |
denotes |
Amendment to clinical research project, Project 90-C-195, January 10, 1992. |
| T3 |
263-530 |
Sentence |
denotes |
Significant increases in lymphocyte adenosine deaminase activity, T cell numbers and immune function have been achieved in the two children with SCID thus far treated with autologous T cells genetically-corrected by retroviral-mediated insertion of a normal ADA gene. |
| T4 |
531-811 |
Sentence |
denotes |
Although the data obtained to date demonstrate that the use of ADA gene corrected peripheral T cells appears to be an effective treatment for ADA(-)SCID, it is theoretically preferable to try to develop a treatment for these children that will result in stem cell gene correction. |
| T5 |
812-1102 |
Sentence |
denotes |
The genetic correction of T cell progenitors with long-term immune reconstituting ability would be more desirable because repeated infusions of genetically altered cells should not be necessary and the generation of a more complete repertoire of T cell specificities might also be possible. |
| T6 |
1103-1225 |
Sentence |
denotes |
Furthermore, the present treatment protocol involves indefinite continuation of enzyme replacement treatment with PEG-ADA. |
| T7 |
1226-1428 |
Sentence |
denotes |
The demonstration of ADA gene expression in the progeny of transduced stem cells may simplify the decision concerning cessation of this very costly enzyme treatment (approximately $250,000/yr./patient). |
| T8 |
1429-1642 |
Sentence |
denotes |
Recent evidence suggests that a small fraction of bone marrow or peripheral blood mononuclear cells bearing the CD34 antigen contains hematopoietic stem cells with both lymphoid and myeloid reconstituting ability. |
| T9 |
1643-1914 |
Sentence |
denotes |
We propose in this amendment to supplement the infusion of human ADA gene-transduced autologous T cells in children with ADA(-)SCID with autologous peripheral blood CD34+ cells transduced with a second, readily distinguishable ADA vector.(ABSTRACT TRUNCATED AT 250 WORDS) |