Id |
Subject |
Object |
Predicate |
Lexical cue |
T1 |
0-217 |
Sentence |
denotes |
Testing the efficacy and safety of BIO101, for the prevention of respiratory deterioration, in patients with COVID-19 pneumonia (COVA study): a structured summary of a study protocol for a randomised controlled trial. |
T2 |
218-229 |
Sentence |
denotes |
OBJECTIVES: |
T3 |
230-413 |
Sentence |
denotes |
As of December, 1st, 2020, coronavirus disease 2019 (COVID-19) caused by SARS-CoV-2, resulted in more than 1 472 917 deaths worldwide and death toll is still increasing exponentially. |
T4 |
414-534 |
Sentence |
denotes |
Many COVID-19 infected people are asymptomatic or experience moderate symptoms and recover without medical intervention. |
T5 |
535-663 |
Sentence |
denotes |
However, older people and those with comorbid hypertension, diabetes, obesity, or heart disease are at higher risk of mortality. |
T6 |
664-956 |
Sentence |
denotes |
Because current therapeutic options for COVID-19 patients are limited specifically for this elderly population at risk, Biophytis is developing BIO101 (20-hydroxyecdysone, a Mas receptor activator) as a new treatment option for managing patients with SARS-CoV-2 infection at the severe stage. |
T7 |
957-1036 |
Sentence |
denotes |
The angiotensin converting enzyme 2 (ACE2) serves as a receptor for SARS-CoV-2. |
T8 |
1037-1178 |
Sentence |
denotes |
Interaction between ACE2 and SARS-CoV2 spike protein seems to alter the function of ACE2, a key player in the renin-angiotensin system (RAS). |
T9 |
1179-1370 |
Sentence |
denotes |
The clinical picture of COVID-19 includes acute respiratory distress syndrome (ARDS), cardiomyopathy, multiorgan dysfunction and shock, all of which might result from an imbalance of the RAS. |
T10 |
1371-1569 |
Sentence |
denotes |
We propose that RAS balance could be restored in COVID-19 patients through MasR activation downstream of ACE2 activity, with 20-hydroxyecdysone (BIO101) a non-peptidic Mas receptor (MasR) activator. |
T11 |
1570-1690 |
Sentence |
denotes |
Indeed, MasR activation by 20-hydroxyecdysone harbours anti-inflammatory, anti-thrombotic, and anti-fibrotic properties. |
T12 |
1691-1934 |
Sentence |
denotes |
BIO101, a 97% pharmaceutical grade 20-hydroxyecdysone could then offer a new therapeutic option by improving the respiratory function and ultimately promoting survival in COVID-19 patients that develop severe forms of this devastating disease. |
T13 |
1935-2118 |
Sentence |
denotes |
Therefore, the objective of this COVA study is to evaluate the safety and efficacy of BIO101, whose active principle is 20-hydroxyecdysone, in COVID-19 patients with severe pneumonia. |
T14 |
2119-2132 |
Sentence |
denotes |
TRIAL DESIGN: |
T15 |
2133-2258 |
Sentence |
denotes |
Randomized, double-blind, placebo-controlled, multi-centre, group sequential and adaptive which will be conducted in 2 parts. |
T16 |
2259-2266 |
Sentence |
denotes |
Part 1: |
T17 |
2267-2448 |
Sentence |
denotes |
Ascertain the safety and tolerability of BIO101 and obtain preliminary indication of the activity of BIO101, in preventing respiratory deterioration in the target population Part 2: |
T18 |
2449-2602 |
Sentence |
denotes |
Re-assessment of the sample size needed for the confirmatory part 2 and confirmation of the effect of BIO101 observed in part 1 in the target population. |
T19 |
2603-2751 |
Sentence |
denotes |
The study is designed as group sequential to allow an efficient run-through, from obtaining an early indication of activity to a final confirmation. |
T20 |
2752-2909 |
Sentence |
denotes |
And adaptive - to allow accumulation of early data and adapt sample size in part 2 in order to inform the final design of the confirmatory part of the trial. |
T21 |
2910-2923 |
Sentence |
denotes |
PARTICIPANTS: |
T22 |
2924-2945 |
Sentence |
denotes |
Inclusion criteria 1. |
T23 |
2946-2950 |
Sentence |
denotes |
Age: |
T24 |
2951-2966 |
Sentence |
denotes |
45 and above 2. |
T25 |
2967-3179 |
Sentence |
denotes |
A confirmed diagnosis of COVID-19 infection, within the last 14 days, prior to randomization, as determined by PCR or other approved commercial or public health assay, in a specimen as specified by the test used. |
T26 |
3180-3182 |
Sentence |
denotes |
3. |
T27 |
3183-3329 |
Sentence |
denotes |
Hospitalized, in observation or planned to be hospitalized due to COVID-19 infection symptoms with anticipated hospitalization duration ≥3 days 4. |
T28 |
3330-3390 |
Sentence |
denotes |
With evidence of pneumonia based on all of the following: a. |
T29 |
3391-3437 |
Sentence |
denotes |
Clinical findings on a physical examination b. |
T30 |
3438-3494 |
Sentence |
denotes |
Respiratory symptoms developed within the past 7 days 5. |
T31 |
3495-3706 |
Sentence |
denotes |
With evidence of respiratory decompensation that started not more than 4 days before start of study medication and present at screening, meeting one of the following criteria, as assessed by healthcare staff: a. |
T32 |
3707-3743 |
Sentence |
denotes |
Tachypnea: ≥25 breaths per minute b. |
T33 |
3744-3778 |
Sentence |
denotes |
Arterial oxygen saturation ≤92% c. |
T34 |
3779-3937 |
Sentence |
denotes |
A special note should be made if there is suspicion of COVID-19-related myocarditis or pericarditis, as the presence of these is a stratification criterion 6. |
T35 |
3938-4001 |
Sentence |
denotes |
Without a significant deterioration in liver function tests: a. |
T36 |
4002-4049 |
Sentence |
denotes |
ALT and AST ≤ 5x upper limit of normal (ULN) b. |
T37 |
4050-4094 |
Sentence |
denotes |
Gamma-glutamyl transferase (GGT) ≤ 5x ULN c. |
T38 |
4095-4121 |
Sentence |
denotes |
Total bilirubin ≤ 5×ULN 7. |
T39 |
4122-4193 |
Sentence |
denotes |
Willing to participate and able to sign an informed consent form (ICF). |
T40 |
4194-4311 |
Sentence |
denotes |
Or, when relevant, a legally authorized representative (LAR) might sign the ICF on behalf of the study participant 8. |
T41 |
4312-4489 |
Sentence |
denotes |
Female participants should be: at least 5 years post-menopausal (i.e., persistent amenorrhea 5 years in the absence of an alternative medical cause) or surgically sterile; OR a. |
T42 |
4490-4542 |
Sentence |
denotes |
Have a negative urine pregnancy test at screening b. |
T43 |
4543-4663 |
Sentence |
denotes |
Be willing to use a contraceptive method as outlined in inclusion criterion 9 from screening to 30 days after last dose. |
T44 |
4664-4666 |
Sentence |
denotes |
9. |
T45 |
4667-5205 |
Sentence |
denotes |
Male participants who are sexually active with a female partner must agree to the use of an effective method of birth control throughout the study and until 3 months after the last administration of the investigational product. (Note: medically acceptable methods of contraception that may be used by the participant and/or partner include combined oral contraceptive, contraceptive vaginal ring, contraceptive injection, intrauterine device, etonogestrel implant, each supplemented with a condom, as well as sterilization and vasectomy). |
T46 |
5206-5209 |
Sentence |
denotes |
10. |
T47 |
5210-5335 |
Sentence |
denotes |
Female participants who are lactating must agree not to breastfeed during the study and up to 14 days after the intervention. |
T48 |
5336-5339 |
Sentence |
denotes |
11. |
T49 |
5340-5522 |
Sentence |
denotes |
Male participants must agree not to donate sperm for the purpose of reproduction throughout the study and until 3 months after the last administration of the investigational product. |
T50 |
5523-5526 |
Sentence |
denotes |
12. |
T51 |
5527-5543 |
Sentence |
denotes |
For France only: |
T52 |
5544-5593 |
Sentence |
denotes |
Being affiliated with a European Social Security. |
T53 |
5594-5615 |
Sentence |
denotes |
Exclusion criteria 1. |
T54 |
5616-5697 |
Sentence |
denotes |
Not needing or not willing to remain in a healthcare facility during the study 2. |
T55 |
5698-5832 |
Sentence |
denotes |
Moribund condition (death likely in days) or not expected to survive for >7 days - due to other and non-COVID-19 related conditions 3. |
T56 |
5833-6018 |
Sentence |
denotes |
Participant on invasive mechanical ventilation via an endotracheal tube, or extracorporeal membrane oxygenation (ECMO), or high-flow Oxygen (delivery of oxygen at a flow of ≥16 L/min.). |
T57 |
6019-6021 |
Sentence |
denotes |
4. |
T58 |
6022-6120 |
Sentence |
denotes |
Participant is not able to take medications by mouth (as capsules or as a powder, mixed in water). |
T59 |
6121-6123 |
Sentence |
denotes |
5. |
T60 |
6124-6158 |
Sentence |
denotes |
Disallowed concomitant medication: |
T61 |
6159-6351 |
Sentence |
denotes |
Consumption of any herbal products containing 20-hydroxyecdysone and derived from Leuzea carthamoides; Cyanotis vaga or Cyanotis arachnoidea is not allowed (e.g. performance enhancing agents). |
T62 |
6352-6354 |
Sentence |
denotes |
6. |
T63 |
6355-6455 |
Sentence |
denotes |
Any known hypersensitivity to any of the ingredients, or excipients of the study medication, BIO101. |
T64 |
6456-6458 |
Sentence |
denotes |
7. |
T65 |
6459-6583 |
Sentence |
denotes |
Renal disease requiring dialysis, or known renal insufficiency (eGFR≤30 mL/min/1.73 m2, based on Cockcroft & Gault formula). |
T66 |
6584-6586 |
Sentence |
denotes |
8. |
T67 |
6587-6605 |
Sentence |
denotes |
In France only: a. |
T68 |
6606-6699 |
Sentence |
denotes |
Non-affiliation to compulsory French social security scheme (beneficiary or right-holder). b. |
T69 |
6700-6743 |
Sentence |
denotes |
Being under tutelage or legal guardianship. |
T70 |
6744-6857 |
Sentence |
denotes |
Participants will be recruited from approximately 30 clinical centres in Belgium, France, the UK, USA and Brazil. |
T71 |
6858-6921 |
Sentence |
denotes |
Maximum patients' participation in the study will last 28 days. |
T72 |
6922-7059 |
Sentence |
denotes |
Follow-up of participants discharged from hospital will be performed through post-intervention phone calls at 14 (± 2) and 60 (± 4) days. |
T73 |
7060-7088 |
Sentence |
denotes |
INTERVENTION AND COMPARATOR: |
T74 |
7089-7256 |
Sentence |
denotes |
Two treatment arms will be tested in this study: interventional arm 350 mg b.i.d. of BIO101 (AP 20-hydroxyecdysone) and placebo comparator arm 350 mg b.i.d of placebo. |
T75 |
7257-7336 |
Sentence |
denotes |
Administration of daily dose is the same throughout the whole treatment period. |
T76 |
7337-7500 |
Sentence |
denotes |
Participants will receive the study medication while hospitalized for up to 28 days or until a clinical endpoint is reached (i.e., 'negative' or 'positive' event). |
T77 |
7501-7603 |
Sentence |
denotes |
Participants who are officially discharged from hospital care will no longer receive study medication. |
T78 |
7604-7618 |
Sentence |
denotes |
MAIN OUTCOMES: |
T79 |
7619-7642 |
Sentence |
denotes |
Primary study endpoint: |
T80 |
7643-7795 |
Sentence |
denotes |
The proportion of participants with 'negative' events up to 28 days. 'Negative' events are defined as respiratory deterioration and all-cause mortality. |
T81 |
7796-7893 |
Sentence |
denotes |
For the purpose of this study, respiratory deterioration will be defined as any of the following: |
T82 |
7894-8012 |
Sentence |
denotes |
Requiring mechanical ventilation (including cases that will not be intubated due to resource restrictions and triage). |
T83 |
8013-8066 |
Sentence |
denotes |
Requiring extracorporeal membrane oxygenation (ECMO). |
T84 |
8067-8147 |
Sentence |
denotes |
Requiring high-flow oxygen defined as delivery of oxygen at a flow of ≥16 L/min. |
T85 |
8148-8289 |
Sentence |
denotes |
Only if the primary endpoint is significant at the primary final analysis the following Key secondary endpoints will be tested in that order: |
T86 |
8290-8422 |
Sentence |
denotes |
Proportion of participants with events of respiratory failure at Day 28 Proportion of participants with 'positive' events at Day 28. |
T87 |
8423-8632 |
Sentence |
denotes |
Proportion of participants with events of all-cause mortality at Day 28 A 'positive' event is defined as the official discharge from hospital care by the department due to improvement in participant condition. |
T88 |
8633-8669 |
Sentence |
denotes |
Secondary and exploratory endpoints: |
T89 |
8670-8880 |
Sentence |
denotes |
In addition, a variety of functional measures and biomarkers (including the SpO2 / FiO2 ratio, viral load and markers related to inflammation, muscles, tissue and the RAS / MAS pathways) will also be collected. |
T90 |
8881-8895 |
Sentence |
denotes |
RANDOMIZATION: |
T91 |
8896-8995 |
Sentence |
denotes |
Randomization is performed using an IBM clinical development IWRS system during the baseline visit. |
T92 |
8996-9085 |
Sentence |
denotes |
Block-permuted randomization will be used to assign eligible participants in a 1:1 ratio. |
T93 |
9086-9210 |
Sentence |
denotes |
In part 1, randomization will be stratified by RAS pathway modulator use (yes/no) and co-morbidities (none vs. 1 and above). |
T94 |
9211-9545 |
Sentence |
denotes |
In Part 2, randomization will be stratified by centre, gender, RAS pathway modulator use (yes/no), co-morbidities (none vs. 1 and above), receiving Continuous Positive Airway Pressure/Bi-level Positive Airway Pressure (CPAP/BiPAP) at study entry (Yes/No) and suspicion of COVID-19 related myocarditis or pericarditis (present or not). |
T95 |
9546-9565 |
Sentence |
denotes |
BLINDING (MASKING): |
T96 |
9566-9666 |
Sentence |
denotes |
Participants, caregivers, and the study team assessing the outcomes are blinded to group assignment. |
T97 |
9667-9796 |
Sentence |
denotes |
All therapeutic units (TU), BIO101 b.i.d. or placebo b.i.d., cannot be distinguished in compliance with the double-blind process. |
T98 |
9797-9876 |
Sentence |
denotes |
An independent data-monitoring committee (DMC) will conduct 2 interim analyses. |
T99 |
9877-9965 |
Sentence |
denotes |
A first one based on the data from part 1 and a second from the data from parts 1 and 2. |
T100 |
9966-10137 |
Sentence |
denotes |
The first will inform about BIO101 safety, to allow the start of recruitment into part 2 followed by an analysis of the efficacy data, to obtain an indication of activity. |
T101 |
10138-10281 |
Sentence |
denotes |
The second interim analysis will inform about the sample size that will be required for part 2, in order to achieve adequate statistical power. |
T102 |
10282-10383 |
Sentence |
denotes |
Numbers to be randomised (sample size) Number of participants randomized: up to 465, in total Part 1: |
T103 |
10384-10441 |
Sentence |
denotes |
50 (to obtain the proof of concept in COVID-19 patients). |
T104 |
10442-10449 |
Sentence |
denotes |
Part 2: |
T105 |
10450-10579 |
Sentence |
denotes |
310, potentially increased by 50% (up to 465, based on interim analysis 2) (to confirm the effects of BIO101 observed in part 1). |
T106 |
10580-10593 |
Sentence |
denotes |
TRIAL STATUS: |
T107 |
10594-10654 |
Sentence |
denotes |
The current protocol Version is V 10.0, dated on 24.09.2020. |
T108 |
10655-10779 |
Sentence |
denotes |
The recruitment that started on September 1st 2020 is ongoing and is anticipated to finish for the whole study by March2021. |
T109 |
10780-10799 |
Sentence |
denotes |
TRIAL REGISTRATION: |
T110 |
10800-10864 |
Sentence |
denotes |
The trial was registered before trial start in trial registries: |
T111 |
10865-10878 |
Sentence |
denotes |
EudraCT , No. |
T112 |
10879-10994 |
Sentence |
denotes |
2020-001498-63, registered May 18, 2020; and Clinicaltrials.gov, identifier NCT04472728 , registered July 15, 2020. |
T113 |
10995-11009 |
Sentence |
denotes |
FULL PROTOCOL: |
T114 |
11010-11118 |
Sentence |
denotes |
The full protocol is attached as an additional file, accessible from the Trials website (Additional file 1). |
T115 |
11119-11299 |
Sentence |
denotes |
In the interest in expediting dissemination of this material, the familiar formatting has been eliminated; this Letter serves as a summary of the key elements of the full protocol. |
T1 |
0-217 |
Sentence |
denotes |
Testing the efficacy and safety of BIO101, for the prevention of respiratory deterioration, in patients with COVID-19 pneumonia (COVA study): a structured summary of a study protocol for a randomised controlled trial. |
T2 |
218-229 |
Sentence |
denotes |
OBJECTIVES: |
T3 |
230-413 |
Sentence |
denotes |
As of December, 1st, 2020, coronavirus disease 2019 (COVID-19) caused by SARS-CoV-2, resulted in more than 1 472 917 deaths worldwide and death toll is still increasing exponentially. |
T4 |
414-534 |
Sentence |
denotes |
Many COVID-19 infected people are asymptomatic or experience moderate symptoms and recover without medical intervention. |
T5 |
535-663 |
Sentence |
denotes |
However, older people and those with comorbid hypertension, diabetes, obesity, or heart disease are at higher risk of mortality. |
T6 |
664-956 |
Sentence |
denotes |
Because current therapeutic options for COVID-19 patients are limited specifically for this elderly population at risk, Biophytis is developing BIO101 (20-hydroxyecdysone, a Mas receptor activator) as a new treatment option for managing patients with SARS-CoV-2 infection at the severe stage. |
T7 |
957-1036 |
Sentence |
denotes |
The angiotensin converting enzyme 2 (ACE2) serves as a receptor for SARS-CoV-2. |
T8 |
1037-1178 |
Sentence |
denotes |
Interaction between ACE2 and SARS-CoV2 spike protein seems to alter the function of ACE2, a key player in the renin-angiotensin system (RAS). |
T9 |
1179-1370 |
Sentence |
denotes |
The clinical picture of COVID-19 includes acute respiratory distress syndrome (ARDS), cardiomyopathy, multiorgan dysfunction and shock, all of which might result from an imbalance of the RAS. |
T10 |
1371-1569 |
Sentence |
denotes |
We propose that RAS balance could be restored in COVID-19 patients through MasR activation downstream of ACE2 activity, with 20-hydroxyecdysone (BIO101) a non-peptidic Mas receptor (MasR) activator. |
T11 |
1570-1690 |
Sentence |
denotes |
Indeed, MasR activation by 20-hydroxyecdysone harbours anti-inflammatory, anti-thrombotic, and anti-fibrotic properties. |
T12 |
1691-1934 |
Sentence |
denotes |
BIO101, a 97% pharmaceutical grade 20-hydroxyecdysone could then offer a new therapeutic option by improving the respiratory function and ultimately promoting survival in COVID-19 patients that develop severe forms of this devastating disease. |
T13 |
1935-2118 |
Sentence |
denotes |
Therefore, the objective of this COVA study is to evaluate the safety and efficacy of BIO101, whose active principle is 20-hydroxyecdysone, in COVID-19 patients with severe pneumonia. |
T14 |
2119-2132 |
Sentence |
denotes |
TRIAL DESIGN: |
T15 |
2133-2258 |
Sentence |
denotes |
Randomized, double-blind, placebo-controlled, multi-centre, group sequential and adaptive which will be conducted in 2 parts. |
T16 |
2259-2266 |
Sentence |
denotes |
Part 1: |
T17 |
2267-2448 |
Sentence |
denotes |
Ascertain the safety and tolerability of BIO101 and obtain preliminary indication of the activity of BIO101, in preventing respiratory deterioration in the target population Part 2: |
T18 |
2449-2602 |
Sentence |
denotes |
Re-assessment of the sample size needed for the confirmatory part 2 and confirmation of the effect of BIO101 observed in part 1 in the target population. |
T19 |
2603-2751 |
Sentence |
denotes |
The study is designed as group sequential to allow an efficient run-through, from obtaining an early indication of activity to a final confirmation. |
T20 |
2752-2909 |
Sentence |
denotes |
And adaptive - to allow accumulation of early data and adapt sample size in part 2 in order to inform the final design of the confirmatory part of the trial. |
T21 |
2910-2923 |
Sentence |
denotes |
PARTICIPANTS: |
T22 |
2924-2945 |
Sentence |
denotes |
Inclusion criteria 1. |
T23 |
2946-2950 |
Sentence |
denotes |
Age: |
T24 |
2951-2966 |
Sentence |
denotes |
45 and above 2. |
T25 |
2967-3179 |
Sentence |
denotes |
A confirmed diagnosis of COVID-19 infection, within the last 14 days, prior to randomization, as determined by PCR or other approved commercial or public health assay, in a specimen as specified by the test used. |
T26 |
3180-3182 |
Sentence |
denotes |
3. |
T27 |
3183-3329 |
Sentence |
denotes |
Hospitalized, in observation or planned to be hospitalized due to COVID-19 infection symptoms with anticipated hospitalization duration ≥3 days 4. |
T28 |
3330-3390 |
Sentence |
denotes |
With evidence of pneumonia based on all of the following: a. |
T29 |
3391-3437 |
Sentence |
denotes |
Clinical findings on a physical examination b. |
T30 |
3438-3494 |
Sentence |
denotes |
Respiratory symptoms developed within the past 7 days 5. |
T31 |
3495-3706 |
Sentence |
denotes |
With evidence of respiratory decompensation that started not more than 4 days before start of study medication and present at screening, meeting one of the following criteria, as assessed by healthcare staff: a. |
T32 |
3707-3743 |
Sentence |
denotes |
Tachypnea: ≥25 breaths per minute b. |
T33 |
3744-3778 |
Sentence |
denotes |
Arterial oxygen saturation ≤92% c. |
T34 |
3779-3937 |
Sentence |
denotes |
A special note should be made if there is suspicion of COVID-19-related myocarditis or pericarditis, as the presence of these is a stratification criterion 6. |
T35 |
3938-4001 |
Sentence |
denotes |
Without a significant deterioration in liver function tests: a. |
T36 |
4002-4049 |
Sentence |
denotes |
ALT and AST ≤ 5x upper limit of normal (ULN) b. |
T37 |
4050-4094 |
Sentence |
denotes |
Gamma-glutamyl transferase (GGT) ≤ 5x ULN c. |
T38 |
4095-4121 |
Sentence |
denotes |
Total bilirubin ≤ 5×ULN 7. |
T39 |
4122-4193 |
Sentence |
denotes |
Willing to participate and able to sign an informed consent form (ICF). |
T40 |
4194-4311 |
Sentence |
denotes |
Or, when relevant, a legally authorized representative (LAR) might sign the ICF on behalf of the study participant 8. |
T41 |
4312-4489 |
Sentence |
denotes |
Female participants should be: at least 5 years post-menopausal (i.e., persistent amenorrhea 5 years in the absence of an alternative medical cause) or surgically sterile; OR a. |
T42 |
4490-4542 |
Sentence |
denotes |
Have a negative urine pregnancy test at screening b. |
T43 |
4543-4663 |
Sentence |
denotes |
Be willing to use a contraceptive method as outlined in inclusion criterion 9 from screening to 30 days after last dose. |
T44 |
4664-4666 |
Sentence |
denotes |
9. |
T45 |
4667-5205 |
Sentence |
denotes |
Male participants who are sexually active with a female partner must agree to the use of an effective method of birth control throughout the study and until 3 months after the last administration of the investigational product. (Note: medically acceptable methods of contraception that may be used by the participant and/or partner include combined oral contraceptive, contraceptive vaginal ring, contraceptive injection, intrauterine device, etonogestrel implant, each supplemented with a condom, as well as sterilization and vasectomy). |
T46 |
5206-5209 |
Sentence |
denotes |
10. |
T47 |
5210-5335 |
Sentence |
denotes |
Female participants who are lactating must agree not to breastfeed during the study and up to 14 days after the intervention. |
T48 |
5336-5339 |
Sentence |
denotes |
11. |
T49 |
5340-5522 |
Sentence |
denotes |
Male participants must agree not to donate sperm for the purpose of reproduction throughout the study and until 3 months after the last administration of the investigational product. |
T50 |
5523-5526 |
Sentence |
denotes |
12. |
T51 |
5527-5543 |
Sentence |
denotes |
For France only: |
T52 |
5544-5593 |
Sentence |
denotes |
Being affiliated with a European Social Security. |
T53 |
5594-5615 |
Sentence |
denotes |
Exclusion criteria 1. |
T54 |
5616-5697 |
Sentence |
denotes |
Not needing or not willing to remain in a healthcare facility during the study 2. |
T55 |
5698-5832 |
Sentence |
denotes |
Moribund condition (death likely in days) or not expected to survive for >7 days - due to other and non-COVID-19 related conditions 3. |
T56 |
5833-6018 |
Sentence |
denotes |
Participant on invasive mechanical ventilation via an endotracheal tube, or extracorporeal membrane oxygenation (ECMO), or high-flow Oxygen (delivery of oxygen at a flow of ≥16 L/min.). |
T57 |
6019-6021 |
Sentence |
denotes |
4. |
T58 |
6022-6120 |
Sentence |
denotes |
Participant is not able to take medications by mouth (as capsules or as a powder, mixed in water). |
T59 |
6121-6123 |
Sentence |
denotes |
5. |
T60 |
6124-6158 |
Sentence |
denotes |
Disallowed concomitant medication: |
T61 |
6159-6351 |
Sentence |
denotes |
Consumption of any herbal products containing 20-hydroxyecdysone and derived from Leuzea carthamoides; Cyanotis vaga or Cyanotis arachnoidea is not allowed (e.g. performance enhancing agents). |
T62 |
6352-6354 |
Sentence |
denotes |
6. |
T63 |
6355-6455 |
Sentence |
denotes |
Any known hypersensitivity to any of the ingredients, or excipients of the study medication, BIO101. |
T64 |
6456-6458 |
Sentence |
denotes |
7. |
T65 |
6459-6583 |
Sentence |
denotes |
Renal disease requiring dialysis, or known renal insufficiency (eGFR≤30 mL/min/1.73 m2, based on Cockcroft & Gault formula). |
T66 |
6584-6586 |
Sentence |
denotes |
8. |
T67 |
6587-6605 |
Sentence |
denotes |
In France only: a. |
T68 |
6606-6699 |
Sentence |
denotes |
Non-affiliation to compulsory French social security scheme (beneficiary or right-holder). b. |
T69 |
6700-6743 |
Sentence |
denotes |
Being under tutelage or legal guardianship. |
T70 |
6744-6857 |
Sentence |
denotes |
Participants will be recruited from approximately 30 clinical centres in Belgium, France, the UK, USA and Brazil. |
T71 |
6858-6921 |
Sentence |
denotes |
Maximum patients' participation in the study will last 28 days. |
T72 |
6922-7059 |
Sentence |
denotes |
Follow-up of participants discharged from hospital will be performed through post-intervention phone calls at 14 (± 2) and 60 (± 4) days. |
T73 |
7060-7088 |
Sentence |
denotes |
INTERVENTION AND COMPARATOR: |
T74 |
7089-7256 |
Sentence |
denotes |
Two treatment arms will be tested in this study: interventional arm 350 mg b.i.d. of BIO101 (AP 20-hydroxyecdysone) and placebo comparator arm 350 mg b.i.d of placebo. |
T75 |
7257-7336 |
Sentence |
denotes |
Administration of daily dose is the same throughout the whole treatment period. |
T76 |
7337-7500 |
Sentence |
denotes |
Participants will receive the study medication while hospitalized for up to 28 days or until a clinical endpoint is reached (i.e., 'negative' or 'positive' event). |
T77 |
7501-7603 |
Sentence |
denotes |
Participants who are officially discharged from hospital care will no longer receive study medication. |
T78 |
7604-7618 |
Sentence |
denotes |
MAIN OUTCOMES: |
T79 |
7619-7642 |
Sentence |
denotes |
Primary study endpoint: |
T80 |
7643-7795 |
Sentence |
denotes |
The proportion of participants with 'negative' events up to 28 days. 'Negative' events are defined as respiratory deterioration and all-cause mortality. |
T81 |
7796-7893 |
Sentence |
denotes |
For the purpose of this study, respiratory deterioration will be defined as any of the following: |
T82 |
7894-8012 |
Sentence |
denotes |
Requiring mechanical ventilation (including cases that will not be intubated due to resource restrictions and triage). |
T83 |
8013-8066 |
Sentence |
denotes |
Requiring extracorporeal membrane oxygenation (ECMO). |
T84 |
8067-8147 |
Sentence |
denotes |
Requiring high-flow oxygen defined as delivery of oxygen at a flow of ≥16 L/min. |
T85 |
8148-8289 |
Sentence |
denotes |
Only if the primary endpoint is significant at the primary final analysis the following Key secondary endpoints will be tested in that order: |
T86 |
8290-8422 |
Sentence |
denotes |
Proportion of participants with events of respiratory failure at Day 28 Proportion of participants with 'positive' events at Day 28. |
T87 |
8423-8632 |
Sentence |
denotes |
Proportion of participants with events of all-cause mortality at Day 28 A 'positive' event is defined as the official discharge from hospital care by the department due to improvement in participant condition. |
T88 |
8633-8669 |
Sentence |
denotes |
Secondary and exploratory endpoints: |
T89 |
8670-8880 |
Sentence |
denotes |
In addition, a variety of functional measures and biomarkers (including the SpO2 / FiO2 ratio, viral load and markers related to inflammation, muscles, tissue and the RAS / MAS pathways) will also be collected. |
T90 |
8881-8895 |
Sentence |
denotes |
RANDOMIZATION: |
T91 |
8896-8995 |
Sentence |
denotes |
Randomization is performed using an IBM clinical development IWRS system during the baseline visit. |
T92 |
8996-9085 |
Sentence |
denotes |
Block-permuted randomization will be used to assign eligible participants in a 1:1 ratio. |
T93 |
9086-9210 |
Sentence |
denotes |
In part 1, randomization will be stratified by RAS pathway modulator use (yes/no) and co-morbidities (none vs. 1 and above). |
T94 |
9211-9545 |
Sentence |
denotes |
In Part 2, randomization will be stratified by centre, gender, RAS pathway modulator use (yes/no), co-morbidities (none vs. 1 and above), receiving Continuous Positive Airway Pressure/Bi-level Positive Airway Pressure (CPAP/BiPAP) at study entry (Yes/No) and suspicion of COVID-19 related myocarditis or pericarditis (present or not). |
T95 |
9546-9565 |
Sentence |
denotes |
BLINDING (MASKING): |
T96 |
9566-9666 |
Sentence |
denotes |
Participants, caregivers, and the study team assessing the outcomes are blinded to group assignment. |
T97 |
9667-9796 |
Sentence |
denotes |
All therapeutic units (TU), BIO101 b.i.d. or placebo b.i.d., cannot be distinguished in compliance with the double-blind process. |
T98 |
9797-9876 |
Sentence |
denotes |
An independent data-monitoring committee (DMC) will conduct 2 interim analyses. |
T99 |
9877-9965 |
Sentence |
denotes |
A first one based on the data from part 1 and a second from the data from parts 1 and 2. |
T100 |
9966-10137 |
Sentence |
denotes |
The first will inform about BIO101 safety, to allow the start of recruitment into part 2 followed by an analysis of the efficacy data, to obtain an indication of activity. |
T101 |
10138-10281 |
Sentence |
denotes |
The second interim analysis will inform about the sample size that will be required for part 2, in order to achieve adequate statistical power. |
T102 |
10282-10383 |
Sentence |
denotes |
Numbers to be randomised (sample size) Number of participants randomized: up to 465, in total Part 1: |
T103 |
10384-10441 |
Sentence |
denotes |
50 (to obtain the proof of concept in COVID-19 patients). |
T104 |
10442-10449 |
Sentence |
denotes |
Part 2: |
T105 |
10450-10579 |
Sentence |
denotes |
310, potentially increased by 50% (up to 465, based on interim analysis 2) (to confirm the effects of BIO101 observed in part 1). |
T106 |
10580-10593 |
Sentence |
denotes |
TRIAL STATUS: |
T107 |
10594-10654 |
Sentence |
denotes |
The current protocol Version is V 10.0, dated on 24.09.2020. |
T108 |
10655-10779 |
Sentence |
denotes |
The recruitment that started on September 1st 2020 is ongoing and is anticipated to finish for the whole study by March2021. |
T109 |
10780-10799 |
Sentence |
denotes |
TRIAL REGISTRATION: |
T110 |
10800-10864 |
Sentence |
denotes |
The trial was registered before trial start in trial registries: |
T111 |
10865-10878 |
Sentence |
denotes |
EudraCT , No. |
T112 |
10879-10994 |
Sentence |
denotes |
2020-001498-63, registered May 18, 2020; and Clinicaltrials.gov, identifier NCT04472728 , registered July 15, 2020. |
T113 |
10995-11009 |
Sentence |
denotes |
FULL PROTOCOL: |
T114 |
11010-11118 |
Sentence |
denotes |
The full protocol is attached as an additional file, accessible from the Trials website (Additional file 1). |
T115 |
11119-11299 |
Sentence |
denotes |
In the interest in expediting dissemination of this material, the familiar formatting has been eliminated; this Letter serves as a summary of the key elements of the full protocol. |